ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2005 | UUUAUGAGGAGCUCUCUGA AAAUACUCCUCGAGAGACU |
1 | 30 | -29 | P. luciferase | NA | NA | NA | ![]() |
|
aspsirna0078 | ACAGUGAUCGGCAUCACCU UGUCACUAGCCGUAGUGGA |
16 | 4 | 12 | APP | Alzheimers disease | c.2010_2011delGAinsTC (p.Lys670_Met671delinsAsnLeu) | rs28186516 | ![]() |