ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna1780 | UUUAUUGGAGAGAGCACGA GAAUAACCUCUCUCGUGCU |
91 | 93 | 2 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1836 | CUUAUUGGAGAGAGUACGA GAAUAACCUCUCUCGUGCU |
89 | 93 | 4 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1844 | CUUAUUGGAGAGAGCAUGA GAAUAACCUCUCUCGUGCU |
77 | 93 | 16 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |