ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2349 | AGUGUAACGGGUUCAGAGG UCACAUUGCGCAAGUCUCC |
23 | NA | NA | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ![]() |
|
aspsirna2367 | AGUGUAAGGCGUUCAGAGG UCACAUUGCGCAAGUCUCC |
NA | NA | 75 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ![]() |
|
aspsirna2374 | AGUGUAACGCGUUGAGAGG UCACAUUGCGCAAGUCUCC |
NA | NA | 80 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ![]() |
|
aspsirna2379 | AGUGUAACGCGUUCAGAGG UCACAUUGCGCAAGUCUCG |
NA | NA | 85 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ![]() |