ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0005 | GAGGGACCGGUGACGAGAU CUCCCUGGCCACUGCUCUA |
0 | 28 | -28 | RyR1 | Central core disease (CCD) | c.14693T>C,p.Ile4898Thr | rs11819217 | ![]() |
|
aspsirna0015 | GAGGGACCGGUGACGAGAU CUCCCUGGCCACUGCUCUA |
0 | 28 | -28 | RyR1 | Central core disease (CCD) | c.14693T>C,p.Ile4898Thr | rs11819217 | ![]() |
|
aspsirna0025 | GAGGGACCGGUGACGAGAU CUCCCUGGCCACUGCUCUA |
0 | 28 | -28 | RyR1 | Malignanat Hyperthermia (MH) | c.14693T>C,p.Ile4898Thr | rs11819217 | ![]() |
|
aspsirna0035 | GAGGGACCGGUGACGAGAU CUCCCUGGCCACUGCUCUA |
0 | 28 | -28 | RyR1 | Malignanat Hyperthermia (MH) | c.14693T>C,p.Ile4898Thr | rs11819217 | ![]() |
|
aspsirna3124 | GAGGGACCGGUGACGAGAU CUCCCUGGCCACUGCUCUA |
10 | 28 | -18 | RyR1 | Malignanat Hyperthermia (MH) | c.14693T>C,p.Ile4898Thr | rs11819217 | ![]() |