| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna0704 | AGCCGAGAGCAGCCGGCUU UCGGCUCUCGUCGGCCGAC |
47 | 78 | -31 | ATXN1 | Spino Cerebellar Ataxia type-1 (SCA-1) | c.589_591CAG(36_38),p.Gln208_His209 | rs19392292 | 
|
