ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna1983 | UUUAUGAGGAUCUCUCUGC AAAUACUCCUAGAGAGACG |
90 | 30 | 60 | P. luciferase | NA | NA | NA | ![]() |
|
aspsirna1949 | CAAAGGGUGAGCGUGGUCC GUUUCCCACUCGCACCAGG |
NA | NA | 60 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1950 | CCAAAGGGUGAGCGUGGUC GGUUUCCCACUCGCACCAG |
NA | NA | 40 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1956 | AUCGGGCCAAAGGGUGAGC UAGCCCGGUUUCCCACUCG |
NA | NA | 3 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1960 | CAAAGGGUGAGCGUGGUCC GUUUCCCACUCGCACCAGG |
NA | NA | 70 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1961 | CCAAAGGGUGAGCGUGGUC GGUUUCCCACUCGCACCAG |
NA | NA | 23 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1967 | AUCGGGCCAAAGGGUGAGC UAGCCCGGUUUCCCACUCG |
NA | NA | 11 | COL6A3 | Dominant ullrich muscular dystrophy | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1971 | CAAAGGGUGAGCGUGGUCA GUUUCCCACUCGCACCAGG |
40 | 30 | 10 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1972 | CCAAAGGGUGAGCGUGGUA GGUUUCCCACUCGCACCAG |
65 | 35 | 30 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna1978 | AUCGGGCCAAAGGGUGAGA UAGCCCGGUUUCCCACUCG |
80 | 54 | 26 | COL6A3 | Congenital muscular dystrophy type Ullrich (UCMD) | (IVS16DS plus 1G-A) in intron 16 | NA | ![]() |
|
aspsirna3580 | UCAGAGAGAUCCUCAUAAA AGUCUCUCUAGGAGUAUUG |
90 | 35 | 55 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |
|
aspsirna3656 | GGUUGGAGGAGAGAUGAUA CCAACCUCCUCUCUACUAG |
90 | 92 | -2 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |