Total number of Results for G1U are 12
Search:
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna1983 UUUAUGAGGAUCUCUCUGC
AAAUACUCCUAGAGAGACG
90 30 60 P. luciferase NA NA NA
US2005/0176045A1
aspsirna1949 CAAAGGGUGAGCGUGGUCC
GUUUCCCACUCGCACCAGG
NA NA 60 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1950 CCAAAGGGUGAGCGUGGUC
GGUUUCCCACUCGCACCAG
NA NA 40 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1956 AUCGGGCCAAAGGGUGAGC
UAGCCCGGUUUCCCACUCG
NA NA 3 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1960 CAAAGGGUGAGCGUGGUCC
GUUUCCCACUCGCACCAGG
NA NA 70 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1961 CCAAAGGGUGAGCGUGGUC
GGUUUCCCACUCGCACCAG
NA NA 23 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1967 AUCGGGCCAAAGGGUGAGC
UAGCCCGGUUUCCCACUCG
NA NA 11 COL6A3 Dominant ullrich muscular dystrophy (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1971 CAAAGGGUGAGCGUGGUCA
GUUUCCCACUCGCACCAGG
40 30 10 COL6A3 Congenital muscular dystrophy type Ullrich (UCMD) (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1972 CCAAAGGGUGAGCGUGGUA
GGUUUCCCACUCGCACCAG
65 35 30 COL6A3 Congenital muscular dystrophy type Ullrich (UCMD) (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna1978 AUCGGGCCAAAGGGUGAGA
UAGCCCGGUUUCCCACUCG
80 54 26 COL6A3 Congenital muscular dystrophy type Ullrich (UCMD) (IVS16DS plus 1G-A) in intron 16 NA
24518369
aspsirna3580 UCAGAGAGAUCCUCAUAAA
AGUCUCUCUAGGAGUAUUG
90 35 55 PPIB/Cyclophilin B PPIB-Related Osteogenesis Imperfecta (Type IX) NA NA
16489337
aspsirna3656 GGUUGGAGGAGAGAUGAUA
CCAACCUCCUCUCUACUAG
90 92 -2 PPIB/Cyclophilin B PPIB-Related Osteogenesis Imperfecta (Type IX) NA NA
16489337
Showing 1 to 12 of 12 entries