ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0694 | CAGCGGGACCUAUCAGGAA GUCGCCCUGGAUAGUCCUG |
70 | 38 | 32 | ATXN3 | Spino Cerebellar Ataxia type-3 (SCA-3) | c.892_894CAG(8_36) (p.Gln298_Gln305=) | rs12895357 | ![]() |