Total number of Results for G1U,G16C are 1
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ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna0694 CAGCGGGACCUAUCAGGAA
GUCGCCCUGGAUAGUCCUG
70 38 32 ATXN3 Spino Cerebellar Ataxia type-3 (SCA-3) c.892_894CAG(8_36) (p.Gln298_Gln305=) rs12895357
22397573
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