Total number of Results for G3C are 13
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ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna2250 GCAUGUUGGAGACUUGCGC
CGUACAACCUCUGAACGCG
90 45 45 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna2279 GCAUGUUGGAGACUUGCGC
CGUACAACCUCUGAACGCG
82 15 67 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna2317 GCAUGUUGGAGACUUGCGC
CGUACAACCUCUGAACGCG
NA NA 20 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna2045 CUCUCCUGUAGCUAAGCCC
GAGAGGACAUCGAUUCGGG
91 45 46 PPIB/Cyclophilin B NA NA NA
US2005/0176045A1
aspsirna0950 CAAAAUCUUAAUGAUACAU
GUUUUAGAAUUACUAUGUA
82 20 62 KRT12 Meesmann epithelial corneal dystrophy (MECD) c.404G>C,p.Arg135Thr rs57218384
23233254
aspsirna3511 CAAAAUCUUAAUGAUACAU
GUUUUAGAAUUACUAUGUA
82 33 49 KRT12 Meesmann epithelial corneal dystrophy (MECD) c.404G>C,p.Arg135Thr rs57218384
23233254
aspsirna0707 GCAUGUUGGAGACUUGCGC
CGUACAACCUCUGAACGCG
92 25 67 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C, p.Gly86Arg rs12191243
16965178
aspsirna0727 GCAUGUUGGAGACUUGCGC
CGUACAACCUCUGAACGCG
92 25 67 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C, p.Gly86Arg rs12191243
16965178
aspsirna0906 UCCAUCCGACAUUGAACUU
AGGUAGGCUGUAACUUGAA
78 NA NA B2M HLA incompatibility c.31G>C,p.Ala11Pro rs10489448
16520945
aspsirna0910 GUGGGAUCGAGACAUCUAA
CACCCUAGCUCUGUAGAUU
40 NA NA B2M HLA incompatibility c.31G>C,p.Ala11Pro rs10489448
16520945
aspsirna0918 UCCAUCCGACAUUGAACUU
AGGUAGGCUGUAACUUGAA
75 NA NA B2M HLA incompatibility c.31G>C,p.Ala11Pro rs10489448
16520945
aspsirna0922 GUGGGAUCGAGACAUCUAA
CACCCUAGCUCUGUAGAUU
45 NA NA B2M HLA incompatibility c.31G>C,p.Ala11Pro rs10489448
16520945
aspsirna3740 AAAGUUGCGCGGAGGAGUU
UUUCAACGCGCCUCCUGAA
90 8 82 PPIB/Cyclophilin B PPIB-Related Osteogenesis Imperfecta (Type IX) NA NA
16489337
Showing 1 to 13 of 13 entries