ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2250 | GCAUGUUGGAGACUUGCGC CGUACAACCUCUGAACGCG |
90 | 45 | 45 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ![]() |
|
aspsirna2279 | GCAUGUUGGAGACUUGCGC CGUACAACCUCUGAACGCG |
82 | 15 | 67 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ![]() |
|
aspsirna2317 | GCAUGUUGGAGACUUGCGC CGUACAACCUCUGAACGCG |
NA | NA | 20 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ![]() |
|
aspsirna2045 | CUCUCCUGUAGCUAAGCCC GAGAGGACAUCGAUUCGGG |
91 | 45 | 46 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna0950 | CAAAAUCUUAAUGAUACAU GUUUUAGAAUUACUAUGUA |
82 | 20 | 62 | KRT12 | Meesmann epithelial corneal dystrophy (MECD) | c.404G>C,p.Arg135Thr | rs57218384 | ![]() |
|
aspsirna3511 | CAAAAUCUUAAUGAUACAU GUUUUAGAAUUACUAUGUA |
82 | 33 | 49 | KRT12 | Meesmann epithelial corneal dystrophy (MECD) | c.404G>C,p.Arg135Thr | rs57218384 | ![]() |
|
aspsirna0707 | GCAUGUUGGAGACUUGCGC CGUACAACCUCUGAACGCG |
92 | 25 | 67 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C, p.Gly86Arg | rs12191243 | ![]() |
|
aspsirna0727 | GCAUGUUGGAGACUUGCGC CGUACAACCUCUGAACGCG |
92 | 25 | 67 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C, p.Gly86Arg | rs12191243 | ![]() |
|
aspsirna0906 | UCCAUCCGACAUUGAACUU AGGUAGGCUGUAACUUGAA |
78 | NA | NA | B2M | HLA incompatibility | c.31G>C,p.Ala11Pro | rs10489448 | ![]() |
|
aspsirna0910 | GUGGGAUCGAGACAUCUAA CACCCUAGCUCUGUAGAUU |
40 | NA | NA | B2M | HLA incompatibility | c.31G>C,p.Ala11Pro | rs10489448 | ![]() |
|
aspsirna0918 | UCCAUCCGACAUUGAACUU AGGUAGGCUGUAACUUGAA |
75 | NA | NA | B2M | HLA incompatibility | c.31G>C,p.Ala11Pro | rs10489448 | ![]() |
|
aspsirna0922 | GUGGGAUCGAGACAUCUAA CACCCUAGCUCUGUAGAUU |
45 | NA | NA | B2M | HLA incompatibility | c.31G>C,p.Ala11Pro | rs10489448 | ![]() |
|
aspsirna3740 | AAAGUUGCGCGGAGGAGUU UUUCAACGCGCCUCCUGAA |
90 | 8 | 82 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |