ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna3325 | AUCCACUGUGUGCACUUCGUC UAGGUGACACACGUGAAGCAG |
80 | 67 | 13 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |