ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna3338 | AUCCAAUGUGUGCACUUCAUC UAGGUUACACACGUGAAGUAG |
95 | 44 | 51 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |
|
aspsirna3427 | AUCCAAUGUGUGCACUUCAUC UAGGUUACACACGUGAAGUAG |
25 | 0 | 25 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |
|
aspsirna3428 | AUCCAAUGUGUGCACUUCAUC UAGGUUACACACGUGAAGUAG |
45 | 0 | 45 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |
|
aspsirna3429 | AUCCAAUGUGUGCACUUCAUC UAGGUUACACACGUGAAGUAG |
40 | 0 | 40 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |
|
aspsirna3430 | AUCCAAUGUGUGCACUUCAUC UAGGUUACACACGUGAAGUAG |
45 | 0 | 45 | HTT | Huntington disease (HD) | NM_002111.7:c.6931T>C | rs362331 | ![]() |