Total number of Results for G4C (A:A clash) are 5
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna2380 ACGCGUUCAGAGGUUGUAC
AGCGCAAGUCUCCAACAUG
NA NA 80 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna2388 ACGCGUUCAGAGGUUGUAC
UGCGCAAGACUCCAACAUG
NA NA 38 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna2389 ACGCGUUCAAAGGUUGUAC
UGCGCAAGUAUCCAACAUG
NA NA 46 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna2392 ACGCGUUCAGAGGUUGUAC
UGCGCAAGUCACCAACAUG
NA NA 23 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna2399 ACGCGUUCAGAGGUUGUAC
UGCGCAAGUCUCCAACAAG
NA NA 60 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1