| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| ASPsiRNA ID | Mutant allele/ASP-siRNA | Efficacy for mutant(%) |
Efficacy for wild (%) |
Relative Difference (%) | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
| aspsirna2380 | ACGCGUUCAGAGGUUGUAC AGCGCAAGUCUCCAACAUG |
NA | NA | 80 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ||
| aspsirna2388 | ACGCGUUCAGAGGUUGUAC UGCGCAAGACUCCAACAUG |
NA | NA | 38 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ||
| aspsirna2389 | ACGCGUUCAAAGGUUGUAC UGCGCAAGUAUCCAACAUG |
NA | NA | 46 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ||
| aspsirna2392 | ACGCGUUCAGAGGUUGUAC UGCGCAAGUCACCAACAUG |
NA | NA | 23 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ||
| aspsirna2399 | ACGCGUUCAGAGGUUGUAC UGCGCAAGUCUCCAACAAG |
NA | NA | 60 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 |