Total number of Results for G4U are 2
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna0041 GAGAUGGGGACAGUACUUC
CUCUACCCCUGUCAUGAAG
70 28 42 HTT Huntington disease (HD) c.5165C>A,c.52CAG(36_39) rs363125
19289118
aspsirna3745 AAAGUUGCGCGGAGGAGUU
UUUCAACGCGCCUCCGCAA
90 38 52 PPIB/Cyclophilin B PPIB-Related Osteogenesis Imperfecta (Type IX) NA NA
16489337