| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna0041 | GAGAUGGGGACAGUACUUC CUCUACCCCUGUCAUGAAG |
70 | 28 | 42 | HTT | Huntington disease (HD) | c.5165C>A,c.52CAG(36_39) | rs363125 | 
|
|
| aspsirna3745 | AAAGUUGCGCGGAGGAGUU UUUCAACGCGCCUCCGCAA |
90 | 38 | 52 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA |
|
