Total number of Results for G5C,U10C are 1
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna0389 CAGAUUUGGACCUGCCAGU
GUCUAAACCUGGACGGUCA
70 0 70 ACVR1 Fibrodysplasia Ossificans Progressiva (FOP) c.1067G>A,p.Gly356Asp rs12191267
22130450