ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2055 | CUCUCCUGUAGCUCAGGCC GAGAGGACAUCGAGUCCGG |
62 | 45 | 17 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna2423 | AACUCCUCCGCGCCACUUU UUGAGGAGGCGCGGUGAAA |
40 | 70 | -30 | KRAS | NA | NA | NA | ![]() |
|
aspsirna3676 | GGUUGGAGGAGAGAUGAUA CCAACCUCCUCUCGACUAU |
90 | 90 | 0 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |