Total number of Results for G7C are 8
Search:
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna2254 GUUGGAGACUUGCGCAAUG
CAACCUCUGAACGCGUUAC
90 50 40 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna2283 GUUGGAGACUUGCGCAAUG
CAACCUCUGAACGCGUUAC
85 50 35 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna2321 GUUGGAGACUUGCGCAAUG
CAACCUCUGAACGCGUUAC
NA NA 15 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna0954 AUCUUAAUGAUACAUUAGC
UAGAAUUACUAUGUAAUCG
83 50 33 KRT12 Meesmann epithelial corneal dystrophy (MECD) c.404G>C,p.Arg135Thr rs57218384
23233254
aspsirna3515 AUCUUAAUGAUACAUUAGC
UAGAAUUACUAUGUAAUCG
83 50 33 KRT12 Meesmann epithelial corneal dystrophy (MECD) c.404G>C,p.Arg135Thr rs57218384
23233254
aspsirna0711 GUUGGAGACUUGCGCAAUG
CAACCUCUGAACGCGUUAC
94 60 34 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C, p.Gly86Arg rs12191243
16965178
aspsirna0731 GUUGGAGACUUGCGCAAUG
CAACCUCUGAACGCGUUAC
94 60 34 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C, p.Gly86Arg rs12191243
16965178
aspsirna3679 GGUUGGAGGAGAGAUGAUA
CCAACCUCCUCUGUACUAU
90 80 10 PPIB/Cyclophilin B PPIB-Related Osteogenesis Imperfecta (Type IX) NA NA
16489337
Showing 1 to 8 of 8 entries