ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna1790 | CUUGUUGGAGAGAGCACGA GAAUAACCUCUCUCGUGCU |
50 | 93 | 43 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1810 | CUUAUUGGGGAGAGCACGA GAAUAACCUCUCUCGUGCU |
53 | 93 | 40 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1818 | CUUAUUGGAGGGAGCACGA GAAUAACCUCUCUCGUGCU |
65 | 93 | 28 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1826 | CUUAUUGGAGAGGGCACGA GAAUAACCUCUCUCGUGCU |
76 | 93 | 17 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1838 | CUUAUUGGAGAGAGCGCGA GAAUAACCUCUCUCGUGCU |
75 | 93 | 18 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1850 | CUUAUUGGAGAGAGCACGG GAAUAACCUCUCUCGUGCU |
85 | 93 | 8 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |