ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna1791 | CUUUUUGGAGAGAGCACGA GAAUAACCUCUCUCGUGCU |
68 | 93 | 25 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1811 | CUUAUUGGUGAGAGCACGA GAAUAACCUCUCUCGUGCU |
15 | 93 | 78 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1819 | CUUAUUGGAGUGAGCACGA GAAUAACCUCUCUCGUGCU |
0 | 93 | 93 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1827 | CUUAUUGGAGAGUGCACGA GAAUAACCUCUCUCGUGCU |
93 | 93 | 0 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1839 | CUUAUUGGAGAGAGCUCGA GAAUAACCUCUCUCGUGCU |
78 | 93 | 15 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1851 | CUUAUUGGAGAGAGCACGU GAAUAACCUCUCUCGUGCU |
90 | 93 | 3 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |