Total number of Results for U10C,G19A are 1
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ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna3576 CAGUGGCUCACCAGAUUAG
GUCACCGAGUGGUCUAAUC
68 14 54 ACVR1 Fibrodysplasia Ossificans Progressiva (FOP) c.617G>A,p.Arg206His rs12191267
US8859752B2
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