ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2076 | CUCUCCAGUAGCUAAGGCC GAGAGGUCAUCGAUUCCGG |
50 | 45 | 5 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna2444 | AACUCCACCGCGCAACUUU UUGAGGUGGCGCGUUGAAA |
26 | 70 | -44 | KRAS | NA | NA | NA | ![]() |
|
aspsirna0667 | AAGUCCAUCCAGCAGCAGC UUCAGGUAGGUCGUCGUCG |
82 | 5 | 77 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |
|
aspsirna0198 | GUGGCCAGGAGGAAGUAAAAUC CACCGGUCCUCCUUCAUUUUAG |
77 | Poor efficacy | High discrimination | MAPT | Frontotemporal dementia and parkinsonism linked to chromosome 17 (FTDP-17) | c.1960G>A,p.Val654Met | rs63750570 | ![]() |