ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0671 | CAGCAGCAGAAGCAGCAGCAGC GUCGUCGUCUUCGUCGUCGUCG |
10 | Lowest effective | Moderate discrimination | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |