ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0261 | ACUAUAGCAUUGCUCAGUA UGAUAUCGUAACGAGUCAU |
62 | 24 | 38 | LRRK2 | Parkinsons disease (PD) | c.6055G>A,p.Gly2019Ser | rs34637584 | ![]() |
|
aspsirna0867 | CAGCUAUGAACAAUGUCCA GUCGAUACUUGUUACAGGU |
NA | 22 | NA | ATXN7 | Spino Cerebellar Ataxia type-7 (SCA-7) | c.88_90CAG(7_17) | rs193922929 | ![]() |