Total number of Results for U1G(S),G17C are 1
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ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna1027 UAGACUUGGGCAAUGUGAC
CUGUGAACCCGUUACACUG
85 5 80 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
18215350
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