Total number of Results for U2C are 7
Search:
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna1986 UUUAUGAGGAUCUCUCUAA
AAAUACUCCUAGAGAGAUU
90 30 60 P. luciferase NA NA NA
US2005/0176045A1
aspsirna3182 GCCCGCACAGUUUCGACAU
CGGGCGUGUCAAAGCUGUA
50 30 20 TP63 Ectrodactyly-Ectodermal Dysplasia-Clefting syndrome 3 (EEC3) p.Arg132His,c.394G>A rs19392114
26891374
aspsirna0596 GCAGGAACUCAAUUCUCAG
CGUCCUUGAGUUAAGAGUC
60 10 50 KRT9 Epidermolytic palmoplantar keratoderma (EPPK) c.488G>A,p.Arg163Gln rs57758262
22402445
aspsirna0333 CAGGCUCCCAGGCAGGGCU
GUCCGAGGGUCCGUCCCGA
75 15 60 COL7A1 Dominant dystrophic epidermolysis bullosa(DDEB) c.6127G>A,p.Gly2043Arg rs12191283
22336946
aspsirna0242 CAAAGAUUGCUGACUACAG
GUUUCUAACGACUGAUGUC
40 20 20 LRRK2 Parkinsons disease (PD) c.6055G>A,p.Gly2019Ser rs34637584
22031823
aspsirna0877 CAGAUCAAGACCCUCAAAA
GUCUAGUUCUGGGAGUUUU
56 42 14 KRT6a Pachyonychia congenita (PC) c.513C>A,p.Asn171Lys rs59685571
17914454
aspsirna1820 AAGCAGCACAAUGAUGAGUAC
UUCGUCGUGUUACUACUCAUG
NA 60 NA Fen1 Werner syndrome NA NA
16113241
Showing 1 to 7 of 7 entries