ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0820 | UUGGAAGUCUGUGCCAUUGUG AACCUUCAGACACGGUAACAC |
57 | 30 | 27 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs362307 | ![]() |
|
aspsirna0822 | UUGGAAGUCUGUGCCAUUGUG AACCUUCAGACACGGUAACAC |
70 | 45 | 25 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs362307 | ![]() |