| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna0381 | AGAUUUGGACCAGGCAGUC UCUAAACCUGGUCCGUCAG |
NA | 0 | NA | ACVR1 | Fibrodysplasia Ossificans Progressiva (FOP) | c.1067G>A,p.Gly356Asp | rs12191267 | 
|
|
| aspsirna0127 | UUGUGCACAACAGCGUCAA AACACGUGUUGUCGCAGUU |
70 | 88 | -18 | PRNP | Prion disease/Creutzfeldt-Jakob disease | c.532G>A,p.Asp178Asn | rs74315403 |
|
|
| aspsirna0163 | UUGUGCACAACAGCGUCAA AACACGUGUUGUCGCAGUU |
70 | 88 | -18 | PRNP | Prion disease/Creutzfeldt-Jakob disease | c.532G>A,p.Asp178Asn | rs74315403 |
|
