ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2004 | UUUAUGAGGAUAUCUCUGA AAAUACUCCUAUAGAGACU |
0 | 30 | -30 | P. luciferase | NA | NA | NA | ![]() |
|
aspsirna2061 | CUCUCCUGUAGAUAAGGCC GAGAGGACAUCUAUUCCGG |
45 | 45 | 0 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna3608 | UCAGAGAGAUCCUCAUAAA AGUCUCUCUAGUAGUAUUU |
90 | 82 | 8 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |