ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0341 | GACAAAGAUGCUGUGGCCGAU CUGUUUCUACGACACCGGCUA |
74 | 10 | 64 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.281G>C,p.Gly94Ala | rs12191243 | ![]() |
|
aspsirna0342 | GACAAAGAUGCUGUGGCCGAU CUGUUUCUACGACACCGGCUA |
74 | 10 | 64 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.281G>C,p.Gly94Ala | rs12191243 | ![]() |