| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna0895 | AGCAGAGUGGCUGAG---AUGA UCGUCUCACCGACUC---UACU |
46 | 5 | 41 | TOR1A | Early onset torsion dystonia (DYT1) | c.907_909delGAG,p.Glu303del | rs72415998 | 
|
|
| aspsirna0896 | GCAGAGUGGCUGAG---AUGAC CGUCUCACCGACUC---UACUG |
67 | 52 | 15 | TOR1A | Early onset torsion dystonia (DYT1) | c.907_909delGAG,p.Glu303del | rs72415998 |
|
|
| aspsirna0897 | AAGCAGAGUGGCUGAGGAG UUCGUCUCACCGACUCCUC |
74 | 70 | 4 | TOR1A | Early onset torsion dystonia (DYT1) | c.907_909delGAG,p.Glu303del | rs72415998 |
|
|
| aspsirna0898 | AGCAGAGUGGCUGAGGAGA UCGUCUCACCGACUCCUCU |
56 | 34 | 22 | TOR1A | Early onset torsion dystonia (DYT1) | c.907_909delGAG,p.Glu303del | rs72415998 |
|
