ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna3167 | UUGCCAGGUUGCAGCUGCUCUU AACGGUCCAACGUCGACGAGAA |
70 | 20 | 50 | HTT | Huntington disease (HD) | rs362306 | rs362306 | ![]() |
|
aspsirna3168 | UUUGGAAGUCUGUGCCCUUGUA AAACCUUCAGACACGGGAACAU |
78 | 20 | 58 | HTT | Huntington disease (HD) | rs362306 | rs362307 | ![]() |
|
aspsirna3169 | UUUGGAAGUCUUCGCCCUUGUA AAACCUUCAGAAGCGGGAACAU |
85 | 33 | 52 | HTT | Huntington disease (HD) | rs362306 | rs362307 | ![]() |
|
aspsirna3175 | UUGCCAGGUUGCAGCUGCUCUU AACGGUCCAACGUCGACGAGAA |
70 | 20 | 50 | HTT | Huntington disease (HD) | rs362306 | rs362306 | ![]() |
|
aspsirna3178 | UUGCCAGGUUGCAGCUGCUCUU AACGGUCCAACGUCGACGAGAA |
90 | 26 | 64 | HTT | Huntington disease (HD) | rs362306 | rs362306 | ![]() |