ASPsiDb_ID | Mutant allele/ASP-siRNA | Mutant efficacy (%) |
Wild efficacy (%) |
Percentage discrimination (%) |
Gene | Disease | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|
ASPsiDb_ID | Mutant allele/ASP-siRNA | Mutant efficacy (%) |
Wild efficacy (%) |
Percentage discrimination (%) |
Gene | Disease | Analysis | Pubmed ID |
aspsirna0340 | GAGUGAUGCAGAAGAAGGG CUCACUACGUCUUCUUCCC |
85 | 10 | 75 | Glucosamine (UDP-N-acetyl)-2-epimerase/N-acetylmannosamine kinase (GNE) | Sialuria |