| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| ASPsiRNA ID | Mutant allele/ASP-siRNA | Efficacy for mutant(%) |
Efficacy for wild (%) |
Relative Difference (%) | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
| aspsirna0559 | GCUCUUCUCCUUCUUAACU CGAGAAGAGGAAGAAUUGA |
34 | 22 | 12 | CHRNA1 | Congenital myasthenic syndrome (SCCMS) | c.737C>T,p.Ser271Phe | rs48335304 | 
|
|
| aspsirna0560 | GAGAACGUCAUCACCGAGUU CUCUUGCAGUAGUGGCUCAA |
NA | NA | NA | DsRed2 | Congenital myasthenic syndrome (SCCMS) | NA | NA |
|
|
| aspsirna0561 | GAGAACGUUAUCACCGAGUU CUCUUGCAAUAGUGGCUCAA |
0 | 0 | 0 | DsRed2 | Congenital myasthenic syndrome (SCCMS) | NA | NA |
|
|
| aspsirna0562 | GAGAACGUCGUCACCGAGUU CUCUUGCAGCAGUGGCUCAA |
76 | 23 | 53 | DsRed2 | Congenital myasthenic syndrome (SCCMS) | NA | NA |
|
|
| aspsirna0563 | GAGAACGUCGCCACCGAGUU CUCUUGCAGCGGUGGCUCAA |
8 | 25 | -17 | DsRed2 | Congenital myasthenic syndrome (SCCMS) | NA | NA |
|
|
| aspsirna0564 | GCUCUUCUUCUUCUUAACU CGAGAAGAAGAAGAAUUGA |
Low efficacy | High efficacy | High discrimination | CHRNA1 | Congenital myasthenic syndrome (SCCMS) | c.737C>T,p.Ser271Phe | rs48335304 |
|