Total number of Results for Early onset torsion dystonia (DYT1) are 9
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)		 Efficacy
for wild (%)		 Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna0895 AGCAGAGUGGCUGAG---AUGA
UCGUCUCACCGACUC---UACU		 46 5 41 TOR1A Early onset torsion dystonia (DYT1) c.907_909delGAG,p.Glu303del rs72415998
18258738
aspsirna0896 GCAGAGUGGCUGAG---AUGAC
CGUCUCACCGACUC---UACUG		 67 52 15 TOR1A Early onset torsion dystonia (DYT1) c.907_909delGAG,p.Glu303del rs72415998
18258738
aspsirna0897 AAGCAGAGUGGCUGAGGAG
UUCGUCUCACCGACUCCUC		 74 70 4 TOR1A Early onset torsion dystonia (DYT1) c.907_909delGAG,p.Glu303del rs72415998
18258738
aspsirna0898 AGCAGAGUGGCUGAGGAGA
UCGUCUCACCGACUCCUCU		 56 34 22 TOR1A Early onset torsion dystonia (DYT1) c.907_909delGAG,p.Glu303del rs72415998
18258738
aspsirna0923 GAGUGGCUGAG---AUGACAUU
CUCACCGACUC---UACUGUAA		 92 58 34 TOR1A Early onset torsion dystonia (DYT1) c.907_909delGAG,p.Glu303del rs72415998
16280588
aspsirna0924 GUGGCUGAG---AUGACAUUUU
CACCGACUC---UACUGUAAAA		 85 19 66 TOR1A Early onset torsion dystonia (DYT1) c.907_909delGAG,p.Glu303del rs72415998
16280588
aspsirna0925 GUGGCUGAG---AUGACAUUUU
CACCGACUC---UACUGUAAAA		 90 12 78 TOR1A Early onset torsion dystonia (DYT1) c.907_909delGAG,p.Glu303del rs72415998
16280588
aspsirna0926 GUGGCUGAG---AUGACAUUUU
CACCGACUC---UACUGUAAAA		 NA NA NA TOR1A Early onset torsion dystonia (DYT1) c.907_909delGAG,p.Glu303del rs72415998
16280588
aspsirna0927 CAGAGUGGCUGAG---AUGACA
GUCUCACCGACUC---UACUGU		 95 15 80 TOR1A Early onset torsion dystonia (DYT1) c.907_909delGAG,p.Glu303del rs72415998
16280588