| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna2212 | AACAGCAGCUGCAGCAGC UUGUCGUCGUCGUCGUCG |
93 | 10 | 83 | ATN-1 | Dentatorubral-pallidoluysian atrophy (DRPLA) | c.1462_1464CAG(90_93) | rs19392293 | 
|
|
| aspsirna2215 | AACAGCAGCAGCUGCAGCAGC UUGUCGUCGUCGUCGUCGUCG |
98 | 40 | 58 | ATN-1 | Dentatorubral-pallidoluysian atrophy (DRPLA) | c.1462_1464CAG(90_93) | rs19392293 |
|
