ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2008 | UUUAUGAGGUUCUCUCUGA AAAUACUCCAAGAGAGACU |
1 | 30 | -29 | P. luciferase | NA | NA | NA | ![]() |
|
aspsirna2065 | CUCUCCUGUUGCUAAGGCC GAGAGGACAACGAUUCCGG |
32 | 45 | -13 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna2947 | CACUAGUAGUAAGUAUAAU GUGAUCAUCAUUCAUAUUA |
45 | 20 | 25 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna2973 | CACUAGUAGUAAGUAUAAU GUGAUCAUCAUUCAUAUUA |
38 | 20 | 18 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna2991 | CACUAGUAGUAAGUAUAAU GUGAUCAUCAUUCAUAUUA |
40 | 20 | 20 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna2993 | CACUAGUAGUAAGUAUAAU GUGAUCAUCAUUCAUAUUA |
50 | 15 | 35 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna3003 | CACUAGUAGUAAGUAUAAU GUGAUCAUCAUUCAUAUUA |
55 | 20 | 35 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna2147 | CAGCAGCUGCAGCAGA-VP GUCGUCGACGUCGUCU-VP |
80 | 24 | 56 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |
|
aspsirna3690 | GGUUGGAGGAGAGAUGAUA CCAACCUCCACUCUACUAU |
90 | 22 | 68 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |