Total number of Results for A16U,A16U(S) are 1
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ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna1035 GAGACUUGGGCAAUGAGAC
CUCAGAACCCGUUACACUG
76 58 18 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
18215350
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