ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0985 | CAGCAGCAGCAGUAGUAGCAG GUCGUCGUCGUCAUCAUCGUC |
78 | 20 | 58 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |
|
aspsirna0989 | CAGCAGCAGCAGUAGUAGCAG GUCGUCGUCGUCAUCAUCGUC |
78 | 20 | 58 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |
|
aspsirna0992 | CAGCAGCAGCAGUAGU GUCGUCGUCGUCAUCAUCGUC |
78 | 25 | 53 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |
|
aspsirna0994 | CAGCAGCAGCAGUAGUA GUCGUCGUCGUCAUCAUCGUC |
78 | 25 | 53 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |
|
aspsirna0996 | CAGCAGCAGCAGUAGU GUCGUCGUCGUCAUCAUCGUC |
70 | 25 | 45 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |
|
aspsirna0998 | CAGCAGCAGCAGUAGUA GUCGUCGUCGUCAUCAUCGUC |
78 | 20 | 58 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 | ![]() |