| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna2202 | CAGCUGCAGCUGCAGCAGC GUCGACGUCGACGUCGUCG |
60 | 40 | 20 | ATN-1 | Dentatorubral-pallidoluysian atrophy (DRPLA) | c.1462_1464CAG(90_93) | rs19392293 | 
|
|
| aspsirna2246 | UUCAGCUGCAGCUGCAGCAGU AAGUCGACGUCGACGUCGUCU |
85 | 30 | 55 | ATN-1 | Dentatorubral-pallidoluysian atrophy (DRPLA) | c.1462_1464CAG(90_93) | rs19392293 |
|
|
| aspsirna2152 | CAGCUGCAGCUGCAGCAGU-P GUCGACGUCGACGUCGUCU-P |
45 | 68 | -23 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 |
|
|
| aspsirna2156 | CAGCUGCAGCUGCAGCAGU-VP GUCGACGUCGACGUCGUCU-VP |
40 | 50 | -10 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 |
|
|
| aspsirna2158 | CAGCUGCAGCUGCAGCAGU-VP GUCGACGUCGACGUCGUCU-VP |
80 | 30 | 50 | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 |
|
