ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2083 | CUCGCCUGUAGCUAAGGCC GAGCGGACAUCGAUUCCGG |
60 | 45 | 15 | PPIB/Cyclophilin B | NA | NA | NA | ![]() |
|
aspsirna2451 | AACGCCUCCGCGCAACUUU UUGCGGAGGCGCGUUGAAA |
0 | 70 | -70 | KRAS | NA | NA | NA | ![]() |
|
aspsirna3714 | GGUUGGAGGAGAGAUGAUA CCACCCUCCUCUCUACUAU |
90 | 78 | 12 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |
|
aspsirna0942 | AUGGCCUUCCUGCAGCAGC UACCGGAAGGACGUCGUCG |
77 | 12 | 65 | AR | Spinal and Bulbar Muscular Atrophy, X-linked 1; SMAX1/Kennedy’s disease | c.172_174CAG(10_36) (p.Gln69_Gln80del)] | rs19392293 | ![]() |