ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2370 | AGUGUAACGGGUUCAGAGG UCACAUUGCGCAAGUCUCC |
NA | NA | 30 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ![]() |
|
aspsirna1779 | GUUAUUGGAGAGAGCACGA GAAUAACCUCUCUCGUGCU |
92 | 93 | 1 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1835 | CUUAUUGGAGAGAGGACGA GAAUAACCUCUCUCGUGCU |
54 | 93 | 39 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |
|
aspsirna1843 | CUUAUUGGAGAGAGCAGGA GAAUAACCUCUCUCGUGCU |
68 | 93 | 25 | CD46 | Hemolytic uremic syndrome | c.104G>A, p.Cys35Tyr | rs12190959 | ![]() |