Total number of Results for G18C are 10
Search:
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna2265 GCGCAAUGUGACUGCUGAC
CGCGUUACACUGACGACUG
85 40 45 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna2294 GCGCAAUGUGACUGCUGAC
CGCGUUACACUGACGACUG
75 60 15 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna2332 GCGCAAUGUGACUGCUGAC
CGCGUUACACUGACGACUG
NA NA 20 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C,p.Gly86Arg rs12191243
US2007/0259827A1
aspsirna0965 ACAUUAGCUUCCUACCUGG
UGUAAUCGAAGGAUGGACC
60 30 30 KRT12 Meesmann epithelial corneal dystrophy (MECD) c.404G>C,p.Arg135Thr rs57218384
23233254
aspsirna3526 ACAUUAGCUUCCUACCUGG
UGUAAUCGAAGGAUGGACC
60 30 30 KRT12 Meesmann epithelial corneal dystrophy (MECD) c.404G>C,p.Arg135Thr rs57218384
23233254
aspsirna0722 GCGCAAUGUGACUGCUGAC
CGCGUUACACUGACGACUG
70 68 2 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C, p.Gly86Arg rs12191243
16965178
aspsirna0742 GCGCAAUGUGACUGCUGAC
CGCGUUACACUGACGACUG
70 68 2 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.256G>C, p.Gly86Arg rs12191243
16965178
aspsirna3723 GGUUGGAGGAGAGAUGAUA
CGAACCUCCUCUCUACUAU
90 95 -5 PPIB/Cyclophilin B PPIB-Related Osteogenesis Imperfecta (Type IX) NA NA
16489337
aspsirna0803 UCGAUUCCAUGUUCAUGAG
AGCUAAGGUACAAGUACUC
50 42 8 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.281G>C,p.Gly94Ala rs12191243
15768029
aspsirna0805 UCGAUUCCAUGUUCAUGAG
AGCUAAGGUACAAGUACUC
50 42 8 SOD1 Amyotrophic Lateral Sclerosis (ALS) c.281G>C,p.Gly94Ala rs12191243
15768029
Showing 1 to 10 of 10 entries