ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2945 | CAUAGUCAUAUCUAAAAGU GUAUCAGUAUAGAUUUUCA |
30 | 20 | 10 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna2950 | UUCUAAAAGACACUAGUAG AAGAUUUUCUGUGAUCAUC |
33 | 20 | 13 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna2963 | GGAUUUAUGAGGAUACAAA CCUAAAUACUCCUAUGUUU |
95 | 15 | 80 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna2971 | CAUAGUCAUAUCUAAAAGU GUAUCAGUAUAGAUUUUCA |
20 | 20 | 0 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna2976 | UUCUAAAAGACACUAGUAG AAGAUUUUCUGUGAUCAUC |
20 | 20 | 0 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna2989 | GGAUUUAUGAGGAUACAAA CCUAAAUACUCCUAUGUUU |
80 | 15 | 65 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna3001 | CAUAGUCAUAUCUAAAAGU GUAUCAGUAUAGAUUUUCA |
70 | 20 | 50 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna3006 | UUCUAAAAGACACUAGUAG AAGAUUUUCUGUGAUCAUC |
80 | 20 | 60 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna3019 | GGAUUUAUGAGGAUACAAA CCUAAAUACUCCUAUGUUU |
90 | 15 | 75 | SNCA | Parkinsons disease (PD) | SNCA locus triplication | NA | ![]() |
|
aspsirna3616 | UCAGAGAGAUCCUCAUAAA AGUCUCUCUUGGAGUAUUU |
90 | 12 | 78 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |