ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0169 | UGAAGUGAAUCUGGAUGCAG ACUUCACUUAGACCUACGUC |
84 | 12 | 72 | APP | Alzheimers disease | c.2010_2011delGAinsTC (p.Lys670_Met671delinsAsnLeu) | rs28186516 | ![]() |
|
aspsirna0170 | UGAAGUGAAUCUGGAUGCAG ACUUCACUUAGACCUACGUC |
60 | 10 | 50 | APP | Alzheimers disease | c.2010_2011delGAinsTC (p.Lys670_Met671delinsAsnLeu) | rs28186516 | ![]() |