Total number of Results for c.5165C>A,c.52CAG(36_39) are 6
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna0041 GAGAUGGGGACAGUACUUC
CUCUACCCCUGUCAUGAAG
70 28 42 HTT Huntington disease (HD) c.5165C>A,c.52CAG(36_39) rs363125
19289118
aspsirna0042 GAGAUGGGGACAGUAAUUC
CUCUACCCCUGUCAUUAAG
70 22 48 HTT Huntington disease (HD) c.5165C>A,c.52CAG(36_39) rs363125
19289118
aspsirna0043 GGACAGUACUUCAACGCUA
CCUGUCAUGAAGUUGCGAU
94 50 44 HTT Huntington disease (HD) c.5165C>A,c.52CAG(36_39) rs363125
19289118
aspsirna0044 GGACAGUAAUUCAACGCUA
CCUGUCAUUAAGUUGCGAU
50 92 -42 HTT Huntington disease (HD) c.5165C>A,c.52CAG(36_39) rs363125
19289118
aspsirna0045 GGACAGUACAUCAACGCUA
CCUGUCAUGUAGUUGCGAU
90 60 30 HTT Huntington disease (HD) c.5165C>A,c.52CAG(36_39) rs363125
19289118
aspsirna0046 GGACAGUAAGUCAACGCUA
CCUGUCAUUCAGUUGCGAU
55 82 -27 HTT Huntington disease (HD) c.5165C>A,c.52CAG(36_39) rs363125
19289118