Total number of Results for Early onset torsion dystonia (DYT1) are 9
ASPsiDb_ID Mutant allele/ASP-siRNA Mutant
efficacy (%)
Wild
efficacy (%)
Percentage
discrimination (%)
Gene Disease Analysis Pubmed ID
ASPsiDb_ID Mutant allele/ASP-siRNA Mutant
efficacy (%)
Wild
efficacy (%)
Percentage
discrimination (%)
Gene Disease Analysis Pubmed ID
aspsirna0895 AGCAGAGUGGCUGAG---AUGA
UCGUCUCACCGACUC---UACU
46 5 41 Torsin family 1, member A (TOR1A) Early onset torsion dystonia (DYT1)
18258738
aspsirna0896 GCAGAGUGGCUGAG---AUGAC
CGUCUCACCGACUC---UACUG
67 52 15 Torsin family 1, member A (TOR1A) Early onset torsion dystonia (DYT1)
18258738
aspsirna0897 AAGCAGAGUGGCUGAGGAG
UUCGUCUCACCGACUCCUC
74 70 4 Torsin family 1, member A (TOR1A) Early onset torsion dystonia (DYT1)
18258738
aspsirna0898 AGCAGAGUGGCUGAGGAGA
UCGUCUCACCGACUCCUCU
56 34 22 Torsin family 1, member A (TOR1A) Early onset torsion dystonia (DYT1)
18258738
aspsirna0923 GAGUGGCUGAG---AUGACAUU
CUCACCGACUC---UACUGUAA
92 58 34 Torsin family 1, member A (TOR1A) Early onset torsion dystonia (DYT1)
16280588
aspsirna0924 GUGGCUGAG---AUGACAUUUU
CACCGACUC---UACUGUAAAA
85 19 66 Torsin family 1, member A (TOR1A) Early onset torsion dystonia (DYT1)
16280588
aspsirna0925 GUGGCUGAG---AUGACAUUUU
CACCGACUC---UACUGUAAAA
90 12 78 Torsin family 1, member A (TOR1A) Early onset torsion dystonia (DYT1)
16280588
aspsirna0926 GUGGCUGAG---AUGACAUUUU
CACCGACUC---UACUGUAAAA
NA NA NA Torsin family 1, member A (TOR1A) Early onset torsion dystonia (DYT1)
16280588
aspsirna0927 CAGAGUGGCUGAG---AUGACA
GUCUCACCGACUC---UACUGU
95 15 80 Torsin family 1, member A (TOR1A) Early onset torsion dystonia (DYT1)
16280588