| ASPsiDb_ID | Mutant allele/ASP-siRNA | Mutant efficacy (%) |
Wild efficacy (%) |
Percentage discrimination (%) |
Gene | Disease | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|
| ASPsiDb_ID | Mutant allele/ASP-siRNA | Mutant efficacy (%) |
Wild efficacy (%) |
Percentage discrimination (%) |
Gene | Disease | Analysis | Pubmed ID |
| aspsirna0556 | CAGAGUGGCU---GAGAUGAC GUCUCACCGA---CUCUACUG |
80 | 45 | 35 | Torsin family 1, member A (TOR1A) | DYT1 dystonia | ||
| aspsirna0557 | CU---GAGAUGACAUUUUUCCCC GA---CUCUACUGUAAAAAGGGG |
4 | 15 | -11 | Torsin family 1, member A (TOR1A) | DYT1 dystonia | ||
| aspsirna0558 | GAGUGGCU---GAGAUGACAUUUUUC CUCACCGA---CUCUACUGUAAAAAG |
0 | 27 | -27 | Torsin family 1, member A (TOR1A) | DYT1 dystonia |