Total number of Results for 12783425 are 3
ASPsiDb_ID Mutant allele/ASP-siRNA Mutant
efficacy (%)
Wild
efficacy (%)
Percentage
discrimination (%)
Gene Disease Analysis Pubmed ID
ASPsiDb_ID Mutant allele/ASP-siRNA Mutant
efficacy (%)
Wild
efficacy (%)
Percentage
discrimination (%)
Gene Disease Analysis Pubmed ID
aspsirna0556 CAGAGUGGCU---GAGAUGAC
GUCUCACCGA---CUCUACUG
80 45 35 Torsin family 1, member A (TOR1A) DYT1 dystonia
12783425
aspsirna0557 CU---GAGAUGACAUUUUUCCCC
GA---CUCUACUGUAAAAAGGGG
4 15 -11 Torsin family 1, member A (TOR1A) DYT1 dystonia
12783425
aspsirna0558 GAGUGGCU---GAGAUGACAUUUUUC
CUCACCGA---CUCUACUGUAAAAAG
0 27 -27 Torsin family 1, member A (TOR1A) DYT1 dystonia
12783425