ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna0061 | GAAGUGAAUCUGGAUGCAGA CUUCACUUAGACCUACGUCU |
42 | 90 | -48 | APP | Alzheimers disease | c.2010_2011delGAinsTC (p.Lys670_Met671delinsAsnLeu) | rs28186516 | ![]() |
|
aspsirna0193 | GAAGUGAAUCUGGAUGCAGA CUUCACUUAGACCUACGUCU |
65 | Poor efficacy | High discrimination | APP | Alzheimers disease | c.2010_2011delGAinsTC (p.Lys670_Met671delinsAsnLeu) | rs28186516 | ![]() |