ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
aspsirna2113 | UUGGCGUAGGCAAGAGUGC AACCGCAUCCGUUCUCACG |
3 | 15 | -12 | KRAS | Cancer | c.35G>T,p.Gly12Val | rs12191352 | ![]() |
|
aspsirna2134 | UUGGCGUAGGCAAGAGUGC AACCGCAUCCGUUCUCACG |
3 | 15 | -12 | KRAS | Cancer | c.35G>T,p.Gly12Val | rs12191352 | ![]() |
|
aspsirna0349 | GUUCCAGCUGGGAUACCUG CAAGGUCGACCCUAUGGAC |
50 | 58 | -8 | COL3A1 | Vascular Ehlers-Danlos Syndrome (vEDs) | c.764G>T,p.Gly255Val | rs58777960 | ![]() |
|
aspsirna1019 | GAGACUUGGGCAAUGUGAC CACUGAACCCGUUACACUG |
85 | 5 | 80 | SOD1 | Amyotrophic Lateral Sclerosis (ALS) | c.256G>C,p.Gly86Arg | rs12191243 | ![]() |
|
aspsirna3722 | GGUUGGAGGAGAGAUGAUA CAAACCUCCUCUCUACUAU |
90 | 93 | -3 | PPIB/Cyclophilin B | PPIB-Related Osteogenesis Imperfecta (Type IX) | NA | NA | ![]() |