Total number of Results for ATN-1 are 49
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna2199 CAGCAGCAGCAGCAGCAGC
GUCGUCGUCGUCGUCGUCG
NA NA NA ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2200 CAGCAGCAGCUGCAGCAGC
GUCGUCGUCGACGUCGUCG
50 25 25 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2201 CAGCAGCAUUUUCAGCAGC
GUCGUCGUAAAAGUCGUCG
80 30 50 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2202 CAGCUGCAGCUGCAGCAGC
GUCGACGUCGACGUCGUCG
60 40 20 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2203 CAGGAGCAGCUGCAGCAGC
GUCCUCGUCGACGUCGUCG
70 33 37 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2204 AACAGCAGCAGCUGCAGCAGC
UUGUCGUCGUCGACGUCGUCG
80 20 60 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2205 AACAGCAGCAGUUGCAGCAGC
UUGUCGUCGUCAACGUCGUCG
83 15 68 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2206 AACAGCAGCAUUUGCAGCAGC
UUGUCGUCGUAAACGUCGUCG
78 5 73 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2207 AACAGCAGCAUUUUCAGCAGC
UUGUCGUCGUAAAAGUCGUCG
90 10 80 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2208 AAGCAGCAUUUGCAGCAG
UUCGUCGUAAACGUCGUC
72 15 57 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2209 AAAGCAGCAGUUUCAGCAGCA
UUUCGUCGUCAAAGUCGUCGU
81 35 46 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2210 AAAGCAGCAGUUUUAGCAGCA
UUUCGUCGUCAAAAUCGUCGU
89 50 39 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2211 AAAUGACGACGCUGGUAUAGC
UUUACUGCUGCGACCAUAUCG
60 40 20 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2212 AACAGCAGCUGCAGCAGC
UUGUCGUCGUCGUCGUCG
93 10 83 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2213 CAGCAGCAGUAGCAGCAGC
GUCGUCGUCUUCGUCGUCG
91 23 68 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2214 CAGCAGCAUCAGCAGCAGC
GUCGUCGUUGUCGUCGUCG
96 43 53 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2215 AACAGCAGCAGCUGCAGCAGC
UUGUCGUCGUCGUCGUCGUCG
98 40 58 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2216 CAGCAGCAGUAGCAGCAGC
GUCGUCGUCUUCGUCGUCG
89 13 76 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2217 CAGCAGCAUCAGCAGCAGC
GUCGUCGUUGUCGUCGUCG
98 34 64 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2218 CAGCAGCAUCUUCAGCAGC
GUCGUCGUUGUUGUCGUCG
75 28 47 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2219 CAGCAGCAGUUUCAGCAGC
GUCGUCGUCUUUGUCGUCG
69 38 31 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2220 CAGCAGCAGCUGCAGCAGC
GUCGUCGUCGACGUCGUCG
65 8 57 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2221 CAGCAGCAGCUGCAGCAGC
GUCGUCGUCGACGUCGUCG
97 10 87 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2222 CAGCAGCAGCUGCAGCAGC
GUCGUCGUCGACGUCGUCG
60 13 47 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2223 CAGCAGCAGCUGCAGCAGC
GUCGUCGUCGACGUCGUCG
58 23 35 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2224 CAGCAGCAGCUGCAGCAGC
GUCGUCGUCGACGUCGUCG
67 30 37 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2225 CAGCAGCAGCUGCAGCAGC
GUCGUCGUCGACGUCGUCG
80 30 50 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2226 CAGCAGCAGCAGCAGCAGC
GUCGUCGUCGUCGUCGUCG
90 70 20 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2227 CAGCAGCAGCAGCAGCAGC
GUCGUCGUCGUCGUCGUCG
70 33 37 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2228 CAGCAGCAGCAGCAGCAGC
GUCGUCGUCGUCGUCGUCG
65 25 40 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2229 UUCAGCAGCAGCUGCAGCAGU
AAGUCGUCGUCGACGUCGUCU
96 30 66 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2230 UUCAGCAGCAGCAGCAGUAGU
AAGUCGUCGUCGUCGUCAUCU
48 20 28 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2231 UUCAGCAGCAGCAGCAUCAGU
AAGUCGUCGUCGUCGUAGUCU
60 10 50 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2232 UUCAGCAGCAGCAGCUGCAGU
AAGUCGUCGUCGUCGACGUCU
30 10 20 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2233 UUCAGCAGCAGCAGUAGCAGU
AAGUCGUCGUCGUCAUCGUCU
50 13 37 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2234 UUCAGCAGCAGCAUCAGCAGU
AAGUCGUCGUCGUAGUCGUCU
70 35 35 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2235 UUCAGCAGCAGCUGCAGCAGU
AAGUCGUCGUCGACGUCGUCU
94 24 70 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2236 UUCAGCAGCAGUAGCAGCAGU
AAGUCGUCGUCAUCGUCGUCU
75 34 41 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2237 UUCAGCAGCAUCAGCAGCAGU
AAGUCGUCGUAGUCGUCGUCU
69 30 39 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2238 UUCAGCAGCUGCAGCAGCAGU
AAGUCGUCGACGUCGUCGUCU
76 26 50 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2239 UUCAGUAGCAGCAGCAGCAGU
AAGUCAUCGUCGUCGUCGUCU
80 18 62 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2240 UUCAGCAGCAGUUGCAGCAGU
AAGUCGUCGUCAACGUCGUCU
67 25 42 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2241 UUCAGCAGCAUUUGCAGCAGU
AAGUCGUCGUAAACGUCGUCU
90 25 65 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2242 UUCAGCAGCAUUUUCAGCAGU
AAGUCGUCGUAAAAGUCGUCU
50 18 32 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2243 UUCAGCAGCAUCUGCAGCAGU
AAGUCGUCGUAGACGUCGUCU
80 45 35 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2244 UUCAGCAGUAGCUGCAGCAGU
AAGUCGUCAUCGACGUCGUCU
60 10 50 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2245 UUCAGCAUCAGCUGCAGCAGU
AAGUCGUAGUCGACGUCGUCU
90 60 30 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2246 UUCAGCUGCAGCUGCAGCAGU
AAGUCGACGUCGACGUCGUCU
85 30 55 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774
aspsirna2247 UUCAGCAGCAGCUGCAGCAGU
AAGUCGUCGUCGACGUCGUCU
87 40 47 ATN-1 Dentatorubral-pallidoluysian atrophy (DRPLA) c.1462_1464CAG(90_93) rs19392293
24981774