| ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
|---|---|---|---|---|---|---|---|---|---|---|
| aspsirna2093 | GUCUCCUGUAGCUAAGGCC CAGAGGACAUCGAUUCCGG |
75 | 45 | 30 | PPIB/Cyclophilin B | NA | NA | NA | 
|
|
| aspsirna0484 | GAAGGUUCUGGACACCAAG CUUCCAAGACCUGUGGUUC |
19 | 10 | 9 | KRT5 | Epidermolysis bullosa simplex (EBS) | c.579C>G, p.Asn193Lys | rs60586163 |
|
|
| aspsirna0522 | GAAGGUUCUGGACACCAAG CUUCCAAGACCUGUGGUUC |
19 | 10 | 9 | KRT5 | Epidermolysis bullosa simplex (EBS) | c.579C>G, p.Asn193Lys | rs60586163 |
|
|
| aspsirna0428 | GUGGUUGGUAAAGCCUCAG CACCAACCAUUUCGGAGUC |
63 | 93 | -30 | PSEN1 | Alzheimers disease | c.811C>G, p.Leu271Val | rs63750886 |
|
|
| aspsirna0871 | GGGGAGACCGCCATGGCGA CCCCUCUGGCGGUTCCGCU |
NA | 20 | NA | HTT | Huntington disease (HD) | c.52CAG(36_39) | rs19392295 |
|
|
| aspsirna0872 | GUCCCGGCAGGUGGUGGAGC CAGGGCCGUCCACCACCUCG |
60 | 15 | 45 | PSEN1 | Alzheimers disease | c.458C>G, p.Leu153Val | 63751441 |
|
|
| aspsirna0874 | GUCCCGGCAGGUGGUGGAGC CAGGGCCGUCCACCACCUCG |
70 | 10 | 60 | PSEN1 | Alzheimers disease | c.458C>G, p.Leu153Val | 63751441 |
|
|
| aspsirna0947 | GAGCAGCAGCAGCAGCAGA CUCGUCGUCGUCGUCGUCU |
50 | 43 | 7 | AR | Spinal and Bulbar Muscular Atrophy, X-linked 1; SMAX1/Kennedy’s disease | c.172_174CAG(10_36) (p.Gln69_Gln80del)] | rs19392293 |
|
